DNA contains the instructions and design for all proteins produced. However, it is RNA that builds proteins based on these instructions. An error at any of the many phases of protein production can lead to disease. Rather than targeting the incorrectly made protein, RNA, as a novel therapeutic drug class, has the potential to address problems at any step of protein production. Furthermore, RNA’s ability to turn genes on and off enables scientists to identify the root origins of diseases. This amplifies RNA’s potential to lead to innovative disease treatments and possible cures.